Archives: 2019-06-19

New clues on tissue damage identified in rheumatoid arthritis and lupus

Research supported by the Accelerating Medicines Partnership (AMP) on Rheumatoid Arthritis and Systemic Lupus Erythematosus (RA/SLE) provides new insights into tissue damage for these autoimmune conditions. Findings include the identification of novel molecular signatures related to immune system signaling in kidney cells that may reflect their active role in disease process; molecular targets, including specific white blood

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The management of risk and investment in cell therapy process development: a case study for neurodegenerative disease

A study was conducted under the UK Regenerative Medicine Platform as part of the work of the Cell Behaviour, Differentiation and Manufacturing Hub. It comprised part of the Pluripotent Stem Cell Platform (PSCP) project funded by the Medical Research Council, the Biotechnology and Biological Sciences Research Council and the Engineering and Physical Sciences Research Council

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How will we pay for the coming generation of potentially curative gene therapies? Bill Cassidy US Senator proposals

We have arrived at a special moment in health care. Innovative, life-changing gene therapies are here that will cure or ease debilitating diseases. Yet these expensive treatments are entering a market structure that was not built to price them. Congress will likely need to play a part in developing a new paradigm for financing such

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Fecal Microbiota for Transplantation: Safety Communication- Risk of Serious Adverse Reactions Due to Transmission of Multi-Drug Resistant Organisms

The FDA is now aware of bacterial infections caused by multi-drug resistant organisms (MDROs) that have occurred due to transmission of a MDRO from use of investigational fecal microbiota for transplantation (FMT): Two immunocompromised adults who received investigational FMT developed invasive infections caused by extended-spectrum beta-lactamase (ESBL)-producing Escherichia coli (E.coli). One of the individuals died. FMT

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RESTORE Community produced a new video for ATMP’s diffusion

Large Scale Research Initiative RESTORE The visionary unifying goal of Large Scale Research Initiative RESTORE is to make the transforming promise associated with Advanced Therapies a reality for the benefit of patients and society. RESTORE sees itself as a “place” where medicine, basic research, technology development and engineering meet, communicate and work together. Through this

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