GENE EDITING – REGENHEALTHSOLUTIONS (RHS)

PIER MARIA FORNASARI
2022-11-07

Novel CRISPR/Cas9-based gene-editing therapy shows promise for patients with transthyretin amyloid cardiomyopathy

A single IV infusion of NTLA-2001, a novel CRISPR/Cas9-based gene editing therapy, significantly reduced circulating transthyretin (TTR) protein levels in patients with ATTR amyloid cardiomyopathy, a progressive and fatal cause of heart failure, according to late-breaking research presented today at the American Heart Association’s Scientific Sessions 2022. The meeting, held in person in Chicago and

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PIER MARIA FORNASARI
2022-09-25

New University of California Irvine-led report Illustrates potential of precision genome editing in treating inherited retinal diseases

Improvements in technology and delivery techniques could revolutionize treatment of genetic disorders of vision In a new paper, University of California, Irvine researchers explain how precision genome editing agents have enabled precise gene correction and disease rescue in inherited retinal diseases (IRDs). The study, titled, “Precision genome editing in the eye,” was published this week

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PIER MARIA FORNASARI
2021-06-05

Genetic base editing shows promise for treatment of sickle cell disease

Sickle cell disease is the most common deadly genetic disorder. It results from a mutation that causes normally pliable red blood cells to become brittle and sickle shaped. This leads to pain, organ damage and early death. A team of scientists led by Mitchell J. Weiss, MD, PhD, and Jonathan Yen, PhD, at St. Jude, and David Liu,

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PIER MARIA FORNASARI
2020-02-15

Gene Editing and AI Can Build New Generation of Low-Cost Health Solutions, Bill Gates Says

Bill Gates calls for reducing health care inequities in a AAAS Annual Meeting plenary address. The number of child deaths around the world has declined by half in the past two decades, but that number could be cut even further with the help of artificial intelligence and gene editing tools, said Bill Gates at the

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PIER MARIA FORNASARI
2019-10-14

Geneticists retract study suggesting first CRISPR babies might die early

Researchers rapidly corrected finding through discussions on social media and preprints. Source Nature A study that raised questions over the future health of the world’s first gene-edited babies has been retracted because of key errors that undermined its conclusion. The research, published in June 2019 in Nature Medicine1, had suggested that people with two copies of a natural genetic mutation

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PIER MARIA FORNASARI
2019-10-07

Carnegie Mellon and Yale Universities Receive NIH Grant To Further innovative, synthetic nucleic acid-based gene editing technique

The peptide nucleic acid-based technique offers an alternative to CRISPR-Cas9 A research team from Carnegie Mellon University and Yale University will advance their innovative, synthetic nucleic acid-based gene editing technique under a new grant from the National Institutes of Health’s (NIH’s) Somatic Cell Genome Editing (SCGE) Program. “Our PNA technique offers a promising avenue for treating — and possibly curing —

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PIER MARIA FORNASARI
2019-09-29

The Future of Genome Editing in European Healthcare Systems

The report, sponsored by ARM, Intellia Therapeutics, and CRISPR Therapeutics, and endorsed by former MEP Maria Teresa Giménez Barbat, discusses the commercial, clinical, regulatory, and ethical landscape and framework for the development of therapeutic for genome editing in Europe.

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PIER MARIA FORNASARI
2019-09-24

Pentagon’s research agency wants to use gene editing to protect troops against chemical and biological weapons

Instead of augmenting super-soldiers, DARPA wants to boost troops’ natural defenses against engineered diseases — and even undo gene-editing altogether. The Pentagon’s research agency wants to explore the possibility of editing a soldier’s genetic makeup to protect against chemical and biological attacks. Defense Advanced Research Projects Agency director Steven Walker said Monday that he believes

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PIER MARIA FORNASARI
2019-08-24

Gene Editing in Patient-derived Heart Cells May Be Useful in FA

Removal of the genetic defect that causes Friedreich’s ataxia (FA) in heart cells derived from a patient with heart disease associated with FA reversed the cells’ abnormal molecular profile, a study shows. This gene-editing strategy could be a useful tool for regenerative medicine aimed at treating heart defects associated with the condition. The study, “Excision of the

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REGENERATIVE AND PERSONALISED MEDICINE

DIGITAL HEALTHCARE

Category GENE EDITING

Novel CRISPR/Cas9-based gene-editing therapy shows promise for patients with transthyretin amyloid cardiomyopathy

New University of California Irvine-led report Illustrates potential of precision genome editing in treating inherited retinal diseases

Genetic base editing shows promise for treatment of sickle cell disease

Gene Editing and AI Can Build New Generation of Low-Cost Health Solutions, Bill Gates Says

Geneticists retract study suggesting first CRISPR babies might die early

Carnegie Mellon and Yale Universities Receive NIH Grant To Further innovative, synthetic nucleic acid-based gene editing technique

The Future of Genome Editing in European Healthcare Systems

Pentagon’s research agency wants to use gene editing to protect troops against chemical and biological weapons

Gene Editing in Patient-derived Heart Cells May Be Useful in FA