FDA Approves First Gene Therapy for Pediatric Patients with Sanfilippo Syndrome Type A

Innovative gene therapy offers a new option for children with a rare, progressive neurodevelopmental disease The U.S. Food and Drug Administration approved Fayuvi (rebisufligene etisparvovec-hopf), the first treatment for pediatric patients with mucopolysaccharidosis type IIIA (MPS IIIA), also known as Sanfilippo syndrome type A., MPS IIIA is a rare inherited disease that progressively damages the

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Healthy Eating Linked to Slower Biological Aging—but there Is no Single “Best” Diet: Study Examines Dietary Habits of About 7,500 Adults

 A study by DZNE finds that healthy eating is associated with slower biological aging—and that there is more than one way to eat healthily. The researchers examined ten dietary patterns considered healthy, including the Mediterranean, Nordic, and a plant-based diet, as well as the DASH diet, which is designed to help lower blood pressure. All

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New York Genome Center researchers find a major brain shift between ages 50 and 75

A single-cell study in Science reveals major shifts in immune cells, genome organization and gene regulation in the aging human hippocampus.  These findings offer critical insights into brain aging with major implications for age-related dementias. Researchers have discovered that the human brain undergoes widespread age-related changes in genome regulation beginning in midlife that may help explain why

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New Study: Blood Test Shows Promise for Detecting Pancreatic Cancer at Its Earliest Stages

PANXEON, which combines multiple biomarkers, also identified a precancerous condition of the pancreas, potentially opening a path to intervention before invasive cancer develops One reason pancreatic cancer remains so deadly is because it’s usually discovered late, after it has spread. Now, a major new study shows that a blood test developed by researchers led by

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Independent Commission led by NHS doctors sets out blueprint to accelerate safe AI adoption in healthcare

New recommendations based on extensive public engagement set out how the NHS could give patients faster access to AI advances with proportionate safeguards to protect patient safety and maintain high levels of trust. The National Commission into the Regulation of AI in Healthcare has today, 10 September 2026, published its recommendations on how the UK

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Human heart regrows muscle cells after heart attack, world-first study shows

New research paves way for novel therapies to reverse heart failure. Pioneering research by experts at the University of Sydney, the Baird Institute and the Royal Prince Alfred Hospital in Sydney has shown that heart muscle cells regrow after a heart attack, opening up the possibility of new regenerative treatments for cardiovascular disease. Following the

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